Saylor Graham-Poarch, 7, was inside the special needs classroom at Silver Rail Elementary when a teenage gunman opened fire ...

WASHINGTON – The Food and Drug Administration published draft guidance on Tuesday that would streamline approvals of some ...

(estivillml/Adobe Stock) It took approximately 4 billion years of cumulative evolution to make modern humans, but it only took us 0.000075 of that immense span to settle the entire globe – including ...

A new review finds that four PAX3 mutations behind dominant blue eyes in cats carry sharply different risks of deafness and ...

EMCITATE is the first and only FDA-approved treatment for peripheral thyrotoxicosis in adults and pediatric patients with MCT8 deficiency in the ...

Atrium Therapeutics, Inc. (Nasdaq: RNA) (the "Company"), a biopharmaceutical company advancing precision cardiology by developing RNA therapeutics targeted to the heart, today announced that the first ...

A case report documents 35 months of oral ivosidenib therapy with partial remission and no adverse events in a man with ...

Three Fred Hutch scientists received research grants from the American Cancer Society to study how mutations in cell ...

Addition continues to progress a novel pipeline of non-viral, LNP-delivered, RNA-only gene-addition therapies for severe, lifelong genetic and ...

Orphan Therapeutics Accelerator (OTXL), a patient-centered non-profit biotech focused on reinitiating development and enabling commercial access to shelved therapies for rare diseases, today announced ...

A new report has uncovered a possible connection between a rare, life-threatening disease and the descendants of Black ...

A 32-year-old woman suffering three strokes within a month was diagnosed with hereditary Thrombotic Thrombocytopenic Purpura ...